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Stocks to Compare Sections All Sections Selected Performance Chart Price & Volume MarketRank Analyst Ratings Sales & Book Value Profitability & Earnings Dividends Debt Ownership Miscellaneous Headlines About Compare NASDAQ:ACAD NASDAQ:ARWR NASDAQ:ASND NASDAQ:IONS NASDAQ:RARE On This Page Performance ChartPrice & VolumeMarketRank™Analyst RatingsSales & Book ValueProfitability & EarningsDividendsDebtOwnershipMiscellaneousHeadlinesAbout Comparison Ideas Stock Ideas Comparative Price Performance Over Time1 day7 days30 days90 days365 daysCompare Price & VolumeCompanyCurrent Price50-Day Moving Average52-Week RangeMarket CapBetaAvg. VolumeToday's VolumeACADACADIA Pharmaceuticals$21.74+6.8%$23.75$13.40▼$26.65$3.43B0.752.46 million shs2.75 million shsARWRArrowhead Pharmaceuticals$38.19+6.2%$27.82$9.57▼$39.42$4.97B1.132.21 million shs1.57 million shsASNDAscendis Pharma A/S$207.12-0.8%$198.44$118.03▼$216.45$12.88B0.41456,768 shs416,732 shsIONSIonis Pharmaceuticals$72.39+1.4%$56.72$23.95▼$73.92$11.38B0.332.13 million shs3.13 million shsRAREUltragenyx Pharmaceutical$33.43+5.5%$29.98$25.81▼$57.99$3.05B0.211.69 million shs1.57 million shsAnalysts Agree—These Gold Picks Outshine the RestUnlock the timeless value of gold with our exclusive 2025 Gold Forecasting Report. Explore why gold remains the ultimate investment for safeguarding wealth against inflation, economic shifts, and global uncertainties. Whether you're planning for future generations or seeking a reliable asset in turbulent times, this report is your essential guide to making informed decisions.Get This Free ReportCompare Price PerformanceCompany1-Day Performance7-Day Performance30-Day Performance90-Day Performance1-Year PerformanceACADACADIA Pharmaceuticals+6.78%+2.02%-11.88%-3.59%+45.81%ARWRArrowhead Pharmaceuticals+6.20%+3.38%+33.21%+102.60%+92.10%ASNDAscendis Pharma A/S-0.76%-1.43%+6.42%+16.88%+62.70%IONSIonis Pharmaceuticals+1.43%+3.47%+18.48%+71.66%+91.31%RAREUltragenyx Pharmaceutical+5.49%+8.33%+15.28%+21.96%-41.47%Compare Price & VolumeCompanyCurrent Price50-Day Moving Average52-Week RangeMarket CapBetaAvg. VolumeToday's VolumeACADACADIA Pharmaceuticals$21.74+6.8%$23.75$13.40▼$26.65$3.43B0.752.46 million shs2.75 million shsARWRArrowhead Pharmaceuticals$38.19+6.2%$27.82$9.57▼$39.42$4.97B1.132.21 million shs1.57 million shsASNDAscendis Pharma A/S$207.12-0.8%$198.44$118.03▼$216.45$12.88B0.41456,768 shs416,732 shsIONSIonis Pharmaceuticals$72.39+1.4%$56.72$23.95▼$73.92$11.38B0.332.13 million shs3.13 million shsRAREUltragenyx Pharmaceutical$33.43+5.5%$29.98$25.81▼$57.99$3.05B0.211.69 million shs1.57 million shsAnalysts Agree—These Gold Picks Outshine the RestUnlock the timeless value of gold with our exclusive 2025 Gold Forecasting Report. Explore why gold remains the ultimate investment for safeguarding wealth against inflation, economic shifts, and global uncertainties. Whether you're planning for future generations or seeking a reliable asset in turbulent times, this report is your essential guide to making informed decisions.Get This Free ReportCompare Price PerformanceCompany1-Day Performance7-Day Performance30-Day Performance90-Day Performance1-Year PerformanceACADACADIA Pharmaceuticals+6.78%+2.02%-11.88%-3.59%+45.81%ARWRArrowhead Pharmaceuticals+6.20%+3.38%+33.21%+102.60%+92.10%ASNDAscendis Pharma A/S-0.76%-1.43%+6.42%+16.88%+62.70%IONSIonis Pharmaceuticals+1.43%+3.47%+18.48%+71.66%+91.31%RAREUltragenyx Pharmaceutical+5.49%+8.33%+15.28%+21.96%-41.47%Compare Analyst ForecastsCompanyConsensus Rating ScoreConsensus RatingConsensus Price Target% Upside from Current PriceACADACADIA Pharmaceuticals 2.65Moderate Buy$29.1233.94% UpsideARWRArrowhead Pharmaceuticals 2.78Moderate Buy$43.1412.97% UpsideASNDAscendis Pharma A/S 2.88Moderate Buy$248.2919.88% UpsideIONSIonis Pharmaceuticals 2.80Moderate Buy$78.288.13% UpsideRAREUltragenyx Pharmaceutical 2.77Moderate Buy$81.50143.79% UpsideCurrent Analyst Ratings BreakdownLatest ARWR, ACAD, ASND, IONS, and RARE Analyst RatingsDateCompanyBrokerageActionRatingPrice TargetDetails10/14/2025ACADACADIA PharmaceuticalsWeiss RatingsSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingReiterated RatingHold (C)10/13/2025ASNDAscendis Pharma A/SCantor FitzgeraldSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingBoost Price TargetOverweight$203.00 ➝ $254.0010/9/2025ASNDAscendis Pharma A/SJPMorgan Chase & Co.Subscribe to MarketBeat All Access for the firm's recommendation accuracy ratingBoost Price TargetOverweight$260.00 ➝ $264.0010/8/2025IONSIonis PharmaceuticalsOppenheimerSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingBoost Price TargetOutperform$84.00 ➝ $90.0010/8/2025ARWRArrowhead PharmaceuticalsWeiss RatingsSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingReiterated RatingSell (D-)10/8/2025ARWRArrowhead PharmaceuticalsHC WainwrightSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingReiterated RatingBuy$80.0010/8/2025ASNDAscendis Pharma A/SWeiss RatingsSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingReiterated RatingSell (D-)10/8/2025IONSIonis PharmaceuticalsNeedham & Company LLCSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingBoost Price TargetBuy$70.00 ➝ $78.0010/8/2025IONSIonis PharmaceuticalsWeiss RatingsSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingReiterated RatingSell (D-)10/8/2025IONSIonis PharmaceuticalsHC WainwrightSubscribe to MarketBeat All Access for the firm's recommendation accuracy ratingReiterated RatingBuy$95.0010/8/2025IONSIonis PharmaceuticalsJPMorgan Chase & Co.Subscribe to MarketBeat All Access for the firm's recommendation accuracy ratingUpgradeNeutral ➝ Overweight$49.00 ➝ $80.00(Data available from 10/16/2022 forward. View 10+ years of historical ratings with our analyst ratings screener.)Compare Sales & Book ValueCompanyAnnual RevenuePrice/SalesCashflowPrice/CashBook ValuePrice/BookACADACADIA Pharmaceuticals$1.02B3.60$0.75 per share28.89$4.40 per share4.94ARWRArrowhead Pharmaceuticals$3.55M1,487.37N/AN/A$1.54 per share24.80ASNDAscendis Pharma A/S$393.54M32.47N/AN/A($1.88) per share-110.17IONSIonis Pharmaceuticals$705M16.37N/AN/A$3.73 per share19.41RAREUltragenyx Pharmaceutical$610.16M5.28N/AN/A$2.76 per share12.11Compare Profitability & EarningsCompanyNet IncomeEPSTrailing P/E RatioForward P/E RatioP/E GrowthNet MarginsReturn on Equity (ROE)Return on Assets (ROA)Next Earnings DateACADACADIA Pharmaceuticals$226.45M$1.3316.3528.617.1621.80%14.69%9.41%11/5/2025 (Estimated)ARWRArrowhead Pharmaceuticals-$599.49M-$1.28N/AN/AN/AN/A-40.91%-11.62%11/25/2025 (Estimated)ASNDAscendis Pharma A/S-$409.12M-$5.16N/A863.00N/A-54.94%N/A-24.31%11/13/2025 (Estimated)IONSIonis Pharmaceuticals-$453.90M-$1.84N/AN/AN/A-28.25%-45.29%-8.99%11/5/2025 (Estimated)RAREUltragenyx Pharmaceutical-$569.18M-$5.53N/AN/AN/A-87.34%-237.48%-37.66%11/4/2025 (Estimated)Latest ARWR, ACAD, ASND, IONS, and RARE EarningsDateQuarterCompanyConsensus EstimateReported EPSBeat/MissGap EPSRevenue EstimateActual RevenueDetails11/13/2025Q3 2025ASNDAscendis Pharma A/S-$0.49N/AN/AN/AN/AN/A11/5/2025Q3 2025ACADACADIA Pharmaceuticals$0.14N/AN/AN/A$276.52 millionN/A11/5/2025Q3 2025IONSIonis Pharmaceuticals-$1.15N/AN/AN/A$131.75 millionN/A11/4/2025Q3 2025RAREUltragenyx Pharmaceutical-$1.23N/AN/AN/A$167.42 millionN/A8/7/2025Q3 2025ARWRArrowhead Pharmaceuticals-$0.94-$1.26-$0.32-$1.26$29.01 million$27.77 million8/7/2025Q2 2025ASNDAscendis Pharma A/S-$1.42-$0.93+$0.49-$0.93$163.17 million$216.28 million8/6/2025Q2 2025ACADACADIA Pharmaceuticals$0.14$0.16+$0.02$0.16$263.07 million$264.57 million8/5/2025Q2 2025RAREUltragenyx Pharmaceutical-$1.27-$1.17+$0.10-$1.17$161.37 million$166.50 million7/30/2025Q2 2025IONSIonis Pharmaceuticals$0.19$0.70+$0.51$0.70$270.90 million$452.00 millionCompare DividendsCompanyAnnual PayoutDividend Yield3-Year Dividend GrowthPayout RatioYears of Consecutive GrowthACADACADIA PharmaceuticalsN/AN/AN/AN/AN/AARWRArrowhead PharmaceuticalsN/AN/AN/AN/AN/AASNDAscendis Pharma A/SN/AN/AN/AN/AN/AIONSIonis PharmaceuticalsN/AN/AN/AN/AN/ARAREUltragenyx PharmaceuticalN/AN/AN/AN/AN/ACompare DebtCompanyDebt-to-Equity RatioCurrent RatioQuick RatioACADACADIA PharmaceuticalsN/A2.912.83ARWRArrowhead Pharmaceuticals0.394.874.87ASNDAscendis Pharma A/SN/A1.020.69IONSIonis Pharmaceuticals0.992.872.86RAREUltragenyx PharmaceuticalN/A2.452.30Compare OwnershipInstitutional OwnershipCompanyInstitutional OwnershipACADACADIA Pharmaceuticals96.71%ARWRArrowhead Pharmaceuticals62.61%ASNDAscendis Pharma A/SN/AIONSIonis Pharmaceuticals93.86%RAREUltragenyx Pharmaceutical97.67%Insider OwnershipCompanyInsider OwnershipACADACADIA Pharmaceuticals26.50%ARWRArrowhead Pharmaceuticals4.30%ASNDAscendis Pharma A/S40.00%IONSIonis Pharmaceuticals2.60%RAREUltragenyx Pharmaceutical5.50%Compare Miscellaneous StatsCompanyEmployeesShares OutstandingFree FloatOptionableACADACADIA Pharmaceuticals510168.71 million124.00 millionOptionableARWRArrowhead Pharmaceuticals400138.26 million132.31 millionOptionableASNDAscendis Pharma A/S1,01761.69 million37.02 millionOptionableIONSIonis Pharmaceuticals1,069159.39 million155.25 millionOptionableRAREUltragenyx Pharmaceutical1,29496.37 million91.07 millionOptionableARWR, ACAD, ASND, IONS, and RARE HeadlinesRecent News About These CompaniesEquities Analysts Set Expectations for RARE FY2029 EarningsOctober 15 at 8:09 AM | marketbeat.comHoward Horn Sells 7,942 Shares of Ultragenyx Pharmaceutical (NASDAQ:RARE) StockOctober 15 at 4:27 AM | insidertrades.comAberdeen Group plc Raises Stock Holdings in Ultragenyx Pharmaceutical Inc. $RAREOctober 15 at 3:42 AM | marketbeat.comVontobel Holding Ltd. Takes Position in Ultragenyx Pharmaceutical Inc. $RAREOctober 15 at 3:24 AM | marketbeat.comInsider Selling: Ultragenyx Pharmaceutical (NASDAQ:RARE) CFO Sells 7,942 Shares of StockOctober 14 at 1:21 PM | marketbeat.comUltragenyx Pharmaceutical Inc. (NASDAQ:RARE) Receives Consensus Rating of "Moderate Buy" from BrokeragesOctober 11, 2025 | marketbeat.comUltragenyx Pharmaceutical Inc. (NASDAQ:RARE) Given Consensus Rating of "Moderate Buy" by BrokeragesOctober 11, 2025 | marketbeat.comBank of America Securities Sticks to Its Buy Rating for Ultragenyx Pharmaceutical (RARE)October 10, 2025 | theglobeandmail.comWeiss Ratings Reiterates Sell (E+) Rating for Ultragenyx Pharmaceutical (NASDAQ:RARE)October 9, 2025 | marketbeat.comBank of America Securities Remains Bullish on Ultragenyx Pharmaceutical (RARE)October 8, 2025 | finance.yahoo.comWealth Enhancement Advisory Services LLC Takes $353,000 Position in Ultragenyx Pharmaceutical Inc. $RAREOctober 8, 2025 | marketbeat.comUltragenyx Pharmaceutical (RARE): Valuation Perspectives Following Regulatory Milestones and Pipeline ProgressOctober 3, 2025 | finance.yahoo.comUltragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)October 3, 2025 | globenewswire.comHow Might Ultragenyx (RARE) Leverage Dealmaking Expertise to Shape Its Long-Term Growth Strategy?October 2, 2025 | finance.yahoo.comAssenagon Boosts Ultragenyx Pharmaceutical Inc. (RARE) Stake by 439% Amid Breakthrough PipelineOctober 2, 2025 | insidermonkey.comUltragenyx Pharmaceutical Inc.: Ultragenyx Appoints Eric Olson as Chief Business Officer and Executive Vice PresidentOctober 1, 2025 | finanznachrichten.deUltragenyx appoints Eric Olson Chief Business OfficerOctober 1, 2025 | msn.comUltragenyx Appoints Eric Olson as Chief Business Officer and Executive Vice PresidentSeptember 30, 2025 | globenewswire.comCantor Fitzgerald Reiterates a Buy Rating on Ultragenyx Pharmaceutical (RARE)September 30, 2025 | msn.comRegeneron nabs FDA label expansion for Ultragenyx-partnered cholesterol drugSeptember 26, 2025 | msn.comUltragenyx Pharmaceutical Inc. (RARE) Presents at Bank of America Global Healthcare Conference 2025 TranscriptSeptember 24, 2025 | seekingalpha.comNew MarketBeat Followers Over TimeMedia Sentiment Over Time Top HeadlinesView All HeadlinesWhy Datavault May Be the Penny AI Stock Investors Have Waited ForBy Nathan Reiff | September 22, 2025After the Fed's Rate Cut, PNC Could See a Mortgage Refinance BoomBy Jordan Chussler | September 21, 2025Memes Are Back: Retail Investors Are Piling Into 3 Quantum StocksBy Dan Schmidt | September 29, 2025Why Wall Street Is Betting Billions on Oklo's Nuclear VisionBy Jeffrey Neal Johnson | September 26, 20253 Defense Stocks Surging as Ukraine Tensions DeepenBy Dan Schmidt | October 5, 2025ARWR, ACAD, ASND, IONS, and RARE Company DescriptionsACADIA Pharmaceuticals NASDAQ:ACAD$21.74 +1.38 (+6.78%) Closing price 10/15/2025 04:00 PM EasternExtended Trading$21.71 -0.03 (-0.14%) As of 10/15/2025 07:26 PM Eastern Extended trading is trading that happens on electronic markets outside of regular trading hours. This is a fair market value extended hours price provided by Polygon.io. Learn more.ACADIA Pharmaceuticals Inc., a biopharmaceutical company, focuses on the development and commercialization innovative medicines that address unmet medical needs in central nervous system (CNS) disorders and rare diseases in the United States. The company offers NUPLAZID (pimavanserin) for the treatment of hallucinations and delusions associated with Parkinson's disease psychosis; and DAYBUE, a novel synthetic analog of the amino-terminal tripeptide of insulin-like growth factor 1 for treatment of Rett Syndrome. It also develops Pimavanserin that is in Phase III ADVANCE-2 study to treat the negative symptoms of schizophrenia; ACP-101 whixh is in Phase III for the treatment of hyperphagia in Prader-Willi syndrome; ACP-204 which is in Phase II for the treatment of Alzheimer's disease psychosis; ACP-2591 that is in Phase I for Rett syndrome and Fragile X syndrome; preclinical antisense oligonucleotide programs; and other programs for neuropsychiatric symptoms. It has a license agreement with Neuren Pharmaceuticals Limited to develop and commercialize trofinetide for Rett syndrome and other indications; and a license and collaboration agreement with Stoke Therapeutics, Inc. to discover, develop and commercialize novel RNA-based medicines for the potential treatment of severe and rare genetic neurodevelopmental diseases of the CNS. The company was formerly known as Receptor Technologies, Inc. and changed its name ACADIA Pharmaceuticals Inc. in 1997. ACADIA Pharmaceuticals Inc. was incorporated in 1993 and is headquartered in San Diego, California.Arrowhead Pharmaceuticals NASDAQ:ARWR$38.19 +2.23 (+6.20%) Closing price 10/15/2025 04:00 PM EasternExtended Trading$38.84 +0.66 (+1.72%) As of 05:32 AM Eastern Extended trading is trading that happens on electronic markets outside of regular trading hours. This is a fair market value extended hours price provided by Polygon.io. Learn more.Arrowhead Pharmaceuticals, Inc. develops medicines for the treatment of intractable diseases in the United States. The company's products in pipeline includes Plozasiran, which is in Phase 2b and one Phase 3 clinical trial to treat hypertriglyceridemia, mixed dyslipidemia, and chylomicronemia syndrome; Zodasiran that is in Phase 2b clinical trial for the treatment of dyslipidemia and hypertriglyceridemia; ARO-PNPLA3, which is in Phase 1 clinical trial to treat patients with non-alcoholic steatohepatitis; ARO-RAGE that is in Phase 1/2a clinical trial to treat inflammatory pulmonary conditions; and ARO-MUC5AC, which is in Phase 1/2a clinical trial to treat muco-obstructive pulmonary diseases. It also develops ARO-MMP7 that is in Phase 1/2a clinical trial for treatment of idiopathic pulmonary fibrosis; ARO-DUX4 for the treatment of facioscapulohumeral muscular dystrophy; ARO-SOD1 for the potential treatment of amyotrophic lateral sclerosis; and ARO-C3, which is in Phase 1/2a clinical trial for the treatment of patients with various complement mediated or complement associated renal diseases. In addition, the company is involved in the development of JNJ-3989, which is in Phase 2 clinical trial to treat chronic hepatitis B virus infection; Olpasiran that is in Phase 3 clinical trial to reduce the production of apolipoprotein A; GSK-4532990 that is in phase 2 clinical trial to treat liver diseases; HZN-457, which is in phase 1 clinical trial to treat uncontrolled gout; and Fazirsiran that is in Phase 3 clinical trial for the treatment for liver disease associated with alpha-1 antitrypsin deficiency. Arrowhead Pharmaceuticals, Inc. has license and research collaboration agreements with Janssen Pharmaceuticals, Inc.; Takeda Pharmaceutical Company Limited; Horizon Therapeutics Ireland DAC; Amgen Inc.; and Glaxosmithkline Intellectual Property (No. 3) Limited. The company was founded in 2003 and is headquartered in Pasadena, California.Ascendis Pharma A/S NASDAQ:ASND$207.12 -1.59 (-0.76%) Closing price 10/15/2025 04:00 PM EasternExtended Trading$212.66 +5.54 (+2.68%) As of 04:36 AM Eastern Extended trading is trading that happens on electronic markets outside of regular trading hours. This is a fair market value extended hours price provided by Polygon.io. Learn more.Ascendis Pharma A/S, a biopharmaceutical company, focuses on developing therapies for unmet medical needs. It offers SKYTROFA for treating patients with growth hormone deficiency (GHD). The company is also developing a pipeline of three independent endocrinology rare disease product candidates in clinical development, as well as focuses on advancing oncology therapeutic candidates. The company was incorporated in 2006 and is headquartered in Hellerup, Denmark.Ionis Pharmaceuticals NASDAQ:IONS$72.39 +1.02 (+1.43%) Closing price 10/15/2025 04:00 PM EasternExtended Trading$71.92 -0.47 (-0.64%) As of 04:00 AM Eastern Extended trading is trading that happens on electronic markets outside of regular trading hours. This is a fair market value extended hours price provided by Polygon.io. Learn more.Ionis Pharmaceuticals, Inc. discovers and develops RNA-targeted therapeutics in the United States. The company offers SPINRAZA for spinal muscular atrophy (SMA) in pediatric and adult patients; TEGSEDI, an antisense injection for the treatment of polyneuropathy caused by hereditary transthyretin amyloidosis in adults; and WAYLIVRA, an antisense medicine for treatment for familial chylomicronemia syndrome (FCS) and familial partial lipodystrophy. It also develops medicines for various indications that are in phase 3 study, including Eplontersen as a monthly self-administered subcutaneous injection to treat all types of ATTR; Olezarsen for patients with FCS and severe hypertriglyceridemia (SHTG); Donidalorsen for patients with hereditary angioedema; ION363 for patients with amyotrophic lateral sclerosis; Tofersen to inhibit the production of superoxide dismutase 1; Pelacarsen for patients with established cardiovascular disease and elevated lipoprotein(a); and Bepirovirsen to inhibit the production of viral proteins associated with hepatitis B virus. In addition, the company develops IONIS-FB-LRx to inhibit the production of complement factor B and the alternative complement pathway; and ION224 to reduce the production of diacylglycerol acyltransferase 2. It has a strategic collaboration with Biogen for the treatment of neurological disorders; and collaboration and license agreement with Metagenomi, Inc, AstraZeneca, Bayer AG, GlaxoSmithKline plc, Novartis, Roche, Swedish Orphan Biovitrum AB, and PTC Therapeutics. The company was incorporated in 1989 and is based in Carlsbad, California.Ultragenyx Pharmaceutical NASDAQ:RARE$33.43 +1.74 (+5.49%) Closing price 10/15/2025 04:00 PM EasternExtended Trading$33.72 +0.29 (+0.85%) As of 04:56 AM Eastern Extended trading is trading that happens on electronic markets outside of regular trading hours. This is a fair market value extended hours price provided by Polygon.io. Learn more.Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for treating long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company's products candidatures include DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX111, an AAV9 gene therapy product candidate for the treatment of patients with Sanfilippo syndrome type A, or MPS IIIA, a rare lysosomal storage disease; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc.; Solid Biosciences Inc.; Regeneron; Abeona; and Daiichi Sankyo Co., Ltd. The company was incorporated in 2010 and is headquartered in Novato, California. 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