Compare Stocks

Comparative Price Performance Over Time

Compare Stocks - Price & Volume

CompanyCurrent Price50-Day Moving Average52-Week RangeMarket CapBetaAvg. VolumeToday's Volume
Journey Medical Co. stock logo
DERM
Journey Medical
$3.51
-0.6%
$3.65
$1.02
$8.11
$69.96M0.78172,260 shs47,705 shs
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
$1.09
+1.9%
$1.29
$0.62
$2.76
$126.95M0.161.59 million shs1.13 million shs
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
$17.55
-0.8%
$13.65
$9.40
$17.89
$666.27M0.63174,098 shs127,605 shs
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
$18.03
$18.03
$5.31
$31.73
$1.42B2.323.17 million shsN/A
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
$22.72
-2.6%
$25.35
$14.89
$32.53
$2.06B1.12709,394 shs401,938 shs
A Guide To High-Short-Interest Stocks Cover

MarketBeat's analysts have just released their top five short plays for May 2024. Learn which stocks have the most short interest and how to trade them. Click the link below to see which companies made the list.

Get This Free Report

Price Performance

Company1-Day Performance7-Day Performance30-Day Performance90-Day Performance1-Year Performance
Journey Medical Co. stock logo
DERM
Journey Medical
-1.12%-2.75%-11.75%-28.97%+352,999,900.00%
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
+4.90%-0.93%-20.15%-20.15%-60.37%
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
+3.03%+5.61%+34.91%+52.98%+25.71%
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
0.00%0.00%0.00%0.00%0.00%
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
+1.52%+2.46%-7.97%-20.92%+11.47%

MarketRank™

CompanyOverall ScoreAnalyst's OpinionShort Interest ScoreDividend StrengthESG ScoreNews and Social Media SentimentCompany OwnershipEarnings & Valuation
Journey Medical Co. stock logo
DERM
Journey Medical
1.887 of 5 stars
3.53.00.00.00.02.50.6
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
3.9666 of 5 stars
3.32.00.04.61.92.50.6
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
3.8045 of 5 stars
0.95.01.71.12.53.32.5
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
N/AN/AN/AN/AN/AN/AN/AN/A
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
4.726 of 5 stars
4.42.00.04.71.94.20.6

Analyst Ratings

CompanyConsensus Rating ScoreConsensus RatingConsensus Price Target% Upside from Current Price
Journey Medical Co. stock logo
DERM
Journey Medical
3.00
Buy$8.50142.17% Upside
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
2.60
Moderate Buy$4.80340.37% Upside
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
2.00
Hold$14.75-15.95% Downside
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
N/AN/AN/AN/A
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
2.89
Moderate Buy$52.13129.42% Upside

Current Analyst Ratings

Latest KPTI, RCKT, DERM, PAHC, and PTLA Analyst Ratings

DateCompanyBrokerageActionRatingPrice TargetDetails
5/10/2024
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
Barclays
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Boost Price TargetUnderweight ➝ Underweight$10.00 ➝ $13.00
5/9/2024
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
HC Wainwright
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Reiterated RatingBuy ➝ Buy$8.00
5/7/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
Needham & Company LLC
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Reiterated RatingBuy ➝ Buy$53.00
4/10/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
Needham & Company LLC
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Reiterated RatingBuy ➝ Buy$53.00
4/2/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
The Goldman Sachs Group
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Initiated CoverageNeutral$39.00
3/1/2024
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
HC Wainwright
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Lower Price TargetBuy ➝ Buy$10.00 ➝ $8.00
3/1/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
UBS Group
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Lower Price TargetBuy ➝ Buy$56.00 ➝ $54.00
2/27/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
JPMorgan Chase & Co.
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Lower Price TargetOverweight ➝ Overweight$55.00 ➝ $50.00
2/27/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
Cantor Fitzgerald
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Reiterated RatingOverweight ➝ Overweight$65.00
2/16/2024
Journey Medical Co. stock logo
DERM
Journey Medical
Alliance Global Partners
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Initiated CoverageBuy$8.50
2/13/2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
Needham & Company LLC
Subscribe to MarketBeat All Access for the recommendation accuracy rating
Reiterated RatingBuy ➝ Buy$53.00
(Data available from 5/10/2021 forward. View 10+ years of historical ratings with our analyst ratings screener.)

Sales & Book Value

CompanyAnnual RevenuePrice/SalesCashflowPrice/CashBook ValuePrice/Book
Journey Medical Co. stock logo
DERM
Journey Medical
$79.18M0.88$0.17 per share20.37$1.05 per share3.34
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
$146.03M0.87N/AN/A($1.19) per share-0.92
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
$977.90M0.73$2.20 per share7.96$6.97 per share2.52
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
$116.64M12.13N/AN/A$1.67 per share10.80
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
N/AN/AN/AN/A$5.46 per shareN/A

Profitability & Earnings

CompanyNet IncomeEPSTrailing P/E RatioForward P/E RatioP/E GrowthNet MarginsReturn on Equity (ROE)Return on Assets (ROA)Next Earnings Date
Journey Medical Co. stock logo
DERM
Journey Medical
-$3.85M-$0.35N/AN/AN/A-4.87%-34.08%-5.00%5/13/2024 (Confirmed)
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
-$143.10M-$1.25N/AN/AN/A-97.99%N/A-50.47%8/7/2024 (Estimated)
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
$32.61M$0.3648.7514.506.071.51%16.67%4.73%9/4/2024 (Estimated)
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
-$290.66M-$4.06N/AN/AN/A-232.73%-267.86%-54.66%N/A
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
-$245.60M-$2.87N/AN/AN/AN/A-51.83%-45.87%8/8/2024 (Estimated)

Latest KPTI, RCKT, DERM, PAHC, and PTLA Earnings

DateQuarterCompanyConsensus EstimateReported EPSBeat/MissGap EPSRevenue EstimateActual RevenueDetails
5/13/2024N/A
Journey Medical Co. stock logo
DERM
Journey Medical
-$0.26N/A+$0.26N/AN/AN/A  
5/6/2024Q1 2024
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
-$0.67-$0.66+$0.01-$0.66N/AN/A
3/21/2024Q4 2023
Journey Medical Co. stock logo
DERM
Journey Medical
N/A-$0.12-$0.12-$0.12$15.80 million$15.26 million
2/29/202412/31/2023
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
-$0.29-$0.36-$0.07-$0.36$33.50 million$33.75 million    
2/26/202412/31/2023
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
-$0.78-$0.64+$0.14-$0.64N/AN/A

Dividends

CompanyAnnual PayoutDividend Yield3-Year Dividend GrowthPayout RatioYears of Consecutive Growth
Journey Medical Co. stock logo
DERM
Journey Medical
N/AN/AN/AN/AN/A
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
N/AN/AN/AN/AN/A
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
$0.482.74%N/A133.33%N/A
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
N/AN/AN/AN/AN/A
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
N/AN/AN/AN/AN/A

Latest KPTI, RCKT, DERM, PAHC, and PTLA Dividends

AnnouncementCompanyPeriodAmountYieldEx-Dividend DateRecord DatePayable Date
5/7/2024
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
Quarterly$0.122.83%6/5/20246/5/20246/26/2024
(Data available from 1/1/2013 forward)

Debt

CompanyDebt-to-Equity RatioCurrent RatioQuick Ratio
Journey Medical Co. stock logo
DERM
Journey Medical
0.72
1.35
1.10
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
N/A
3.37
3.32
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
1.66
3.12
1.60
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
4.77
4.87
4.82
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
0.04
7.80
7.80

Ownership

Miscellaneous

CompanyEmployeesShares OutstandingFree FloatOptionable
Journey Medical Co. stock logo
DERM
Journey Medical
4119.93 million16.06 millionN/A
Karyopharm Therapeutics Inc. stock logo
KPTI
Karyopharm Therapeutics
325116.47 million111.46 millionOptionable
Phibro Animal Health Co. stock logo
PAHC
Phibro Animal Health
1,92040.50 million20.23 millionOptionable
Portola Pharmaceuticals, Inc. stock logo
PTLA
Portola Pharmaceuticals
32478.48 millionN/AOptionable
Rocket Pharmaceuticals, Inc. stock logo
RCKT
Rocket Pharmaceuticals
26890.75 million62.53 millionOptionable

KPTI, RCKT, DERM, PAHC, and PTLA Headlines

SourceHeadline
Q2 2024 EPS Estimates for Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) Decreased by Leerink PartnrsQ2 2024 EPS Estimates for Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) Decreased by Leerink Partnrs
marketbeat.com - May 10 at 7:06 AM
Rocket Pharmaceuticals Presents Positive Data from LV Hematology Portfolio at the 27th Annual Meeting of the American Society of Gene and Cell Therapy (ASGCT)Rocket Pharmaceuticals Presents Positive Data from LV Hematology Portfolio at the 27th Annual Meeting of the American Society of Gene and Cell Therapy (ASGCT)
businesswire.com - May 10 at 6:00 AM
Pet Pals: Roscoe RocketPet Pals: Roscoe Rocket
wlos.com - May 9 at 9:53 AM
Cavs at Celtics, Game 2 | Rocket Mortgage Game PreviewCavs at Celtics, Game 2 | Rocket Mortgage Game Preview
nba.com - May 9 at 9:53 AM
Equities Analysts Issue Forecasts for Rocket Pharmaceuticals, Inc.s Q2 2024 Earnings (NASDAQ:RCKT)Equities Analysts Issue Forecasts for Rocket Pharmaceuticals, Inc.'s Q2 2024 Earnings (NASDAQ:RCKT)
americanbankingnews.com - May 9 at 6:36 AM
Rocket Pharmaceuticals (NASDAQ:RCKT) Stock Rating Reaffirmed by Needham & Company LLCRocket Pharmaceuticals (NASDAQ:RCKT) Stock Rating Reaffirmed by Needham & Company LLC
americanbankingnews.com - May 9 at 6:00 AM
Lockheed Martin Gets $861.3M U.S. Army Rocket-System PactLockheed Martin Gets $861.3M U.S. Army Rocket-System Pact
marketwatch.com - May 8 at 6:51 PM
Israel Reopens Key Crossing for Aid to Enter Gaza That Was Closed Over Weekend Rocket AttackIsrael Reopens Key Crossing for Aid to Enter Gaza That Was Closed Over Weekend Rocket Attack
usnews.com - May 8 at 3:26 AM
Optimistic Outlook for Rocket Pharmaceuticals with Advancing Pipeline and Solid FinancialsOptimistic Outlook for Rocket Pharmaceuticals with Advancing Pipeline and Solid Financials
markets.businessinsider.com - May 8 at 3:26 AM
Rocket Knight Adventures: Re-Sparked! launches June 11Rocket Knight Adventures: Re-Sparked! launches June 11
gematsu.com - May 7 at 5:25 PM
Rocket Knight Adventures: Re-Sparked Collection - Official Pre-Order TrailerRocket Knight Adventures: Re-Sparked Collection - Official Pre-Order Trailer
msn.com - May 7 at 5:25 PM
Rockets (RCKT) Q1 Loss Narrower Than Expected, Sales NilRocket's (RCKT) Q1 Loss Narrower Than Expected, Sales Nil
zacks.com - May 7 at 12:31 PM
Rocket Pharmaceuticals (NASDAQ:RCKT) Releases  Earnings Results, Beats Estimates By $0.01 EPSRocket Pharmaceuticals (NASDAQ:RCKT) Releases Earnings Results, Beats Estimates By $0.01 EPS
marketbeat.com - May 7 at 8:52 AM
Needham & Company LLC Reaffirms Buy Rating for Rocket Pharmaceuticals (NASDAQ:RCKT)Needham & Company LLC Reaffirms Buy Rating for Rocket Pharmaceuticals (NASDAQ:RCKT)
marketbeat.com - May 7 at 8:09 AM
RCKT Stock Earnings: Rocket Pharmaceuticals Beats EPS for Q1 2024RCKT Stock Earnings: Rocket Pharmaceuticals Beats EPS for Q1 2024
investorplace.com - May 6 at 10:08 PM
Rocket Pharmaceuticals GAAP EPS of -$0.66 beats by $0.01Rocket Pharmaceuticals GAAP EPS of -$0.66 beats by $0.01
msn.com - May 6 at 9:22 PM
Rocket rookies ride ups and downs of rollercoaster seasonRocket rookies ride ups and downs of rollercoaster season
nhl.com - May 6 at 4:22 PM
Rickie Fowler returning for 2024 Rocket Mortgage Classic in Detroit, tickets on sale nowRickie Fowler returning for 2024 Rocket Mortgage Classic in Detroit, tickets on sale now
msn.com - May 6 at 4:22 PM
Rocket Companies Hires First Chief Technology OfficerRocket Companies Hires First Chief Technology Officer
nationalmortgageprofessional.com - May 6 at 4:22 PM
Rocket hires new CTO to lead artificial intelligence pushRocket hires new CTO to lead artificial intelligence push
crainsdetroit.com - May 6 at 4:22 PM
Rocket Pharmaceuticals Reports First Quarter 2024 Financial Results and Highlights Recent ProgressRocket Pharmaceuticals Reports First Quarter 2024 Financial Results and Highlights Recent Progress
businesswire.com - May 6 at 4:01 PM
Rocket Man ($ROKM) Anti-bearish Missile ROKM-69 Reaches 3,250x Since LaunchRocket Man ($ROKM) Anti-bearish Missile ROKM-69 Reaches 3,250x Since Launch
coingape.com - May 6 at 10:05 AM
3,000+ show up for Cleveland Cavaliers’ watch party at Rocket Mortgage FieldHouse (photos)3,000+ show up for Cleveland Cavaliers’ watch party at Rocket Mortgage FieldHouse (photos)
msn.com - May 4 at 2:25 AM
Fortnite Rocket Racing: How to Unlock Free Star Wars CosmeticsFortnite Rocket Racing: How to Unlock Free Star Wars Cosmetics
gameranx.com - May 3 at 9:25 PM

New MarketBeat Followers Over Time

Media Sentiment Over Time

Company Descriptions

Journey Medical logo

Journey Medical

NASDAQ:DERM
Journey Medical Corporation focuses on the development and commercialization of pharmaceutical products for the treatment of dermatological conditions in the United States. The company's marketed products include Qbrexza, a medicated cloth towelette for the treatment of primary axillary hyperhidrosis; Accutane, an oral isotretinoin drug to treat severe recalcitrant nodular acne; and Amzeeq, a topical formulation of minocycline for the treatment of inflammatory lesions of non-nodular moderate to severe acne vulgaris. It also offers Zilxi, a topical minocycline treatment for inflammatory lesions of rosacea; Exelderm cream and solution an antifungal intended for topical use; Targadox, an oral doxycycline drug for adjunctive therapy for severe acne; and Luxamend, a water-based emulsion formulated to provide a moist healing environment for superficial wounds; minor cuts or scrapes; dermal ulcers; donor sites; first- and second-degree burns, including sunburns; and radiation dermatitis. In addition, the company sells sulconazole nitrate cream and solution indicated for the treatment of tinea cruris, tinea corporis, and tinea versicolor; and doxycycline hyclate tablets, as an adjunctive therapy for severe acne. The company was formerly known as Coronado Dermatology, Inc. and changed its name to Journey Medical Corporation. Journey Medical Corporation was incorporated in 2014 and is headquartered in Scottsdale, Arizona. Journey Medical Corporation is a subsidiary of Fortress Biotech, Inc.
Karyopharm Therapeutics logo

Karyopharm Therapeutics

NASDAQ:KPTI
Karyopharm Therapeutics Inc., a commercial-stage pharmaceutical company, discovers, develops, and commercializes drugs directed against nuclear export for the treatment of cancer and other diseases in the United States. The company discovers, develops, and commercializes novel and small molecule Selective Inhibitor of Nuclear Export (SINE) compounds that inhibit the nuclear export protein exportin 1 (XPO1). Its lead compound, include XPOVIO in combination with bortezomib and dexamethasone for the treatment of adult patients with multiple myeloma; in combination with dexamethasone for the treatment of adult patients with relapsed or refractory multiple myeloma; and for the treatment of adult patients with relapsed or refractory diffuse large B-cell lymphoma (DLBCL). It also developing Selinexor for treating hematological and solid tumor malignancies, including multiple myeloma, endometrial cancer, myelofibrosis, and DLBCL; and ELTANEXOR for treating Myelodysplastic Neoplasms, as well as verdinexor, KPT-9274, and IL-12 compounds. The company has license agreement with Menarini Group to develop and commercialize selinexor for human oncology indications; license agreement with Antengene Therapeutics Limited to develop and commercialize selinexor, eltanexor, and KPT-9274 for the treatment and/or prevention of human oncology indications, as well as verdinexor for the diagnosis, treatment, and/or prevention of human non-oncology indications; and distribution agreement for the commercialization of XPOVIO with FORUS Therapeutics Inc. Further, it has a collaboration with Bristol Myers Squibb company to evaluate novel cereblon E3 ligase modulator agent mezigdomide in combination with Selinexor in patients with relapsed/refractory multiple myeloma. Karyopharm Therapeutics Inc. was incorporated in 2008 and is headquartered in Newton, Massachusetts.
Phibro Animal Health logo

Phibro Animal Health

NASDAQ:PAHC
Phibro Animal Health Corporation operates as an animal health and mineral nutrition company in the United States, Israel, Brazil, Ireland, and internationally. It operates through three segments: Animal Health, Mineral Nutrition, and Performance Products. The company develops, manufactures, and markets various products for food and companion animals including poultry, swine, beef and dairy cattle, aquaculture, and dogs. It also offers animal health products, such as antibacterials, anticoccidials, nutritional specialty, and vaccines and vaccine adjuvants for animal's health and performance, food safety, and animal welfare; and engages in development, manufacturing, and marketing of microbial and bioproducts for various applications serving animal health and nutrition, industrial, environmental, and agricultural customers. In addition, the company develops, manufactures, and markets conventionally licensed and autogenous vaccine products, as well as adjuvants for animal vaccine manufacturers. Further, it provides formulations and concentrations of trace minerals, such as zinc, manganese, copper, iron, and other compounds to fortify the daily feed requirements of their livestock's diets and maintain optimal balance of trace elements in animals. Additionally, the company offers specialty ingredients for personal care, industrial chemical, and chemical catalyst industries. It sells its animal health and mineral nutrition products through local sales offices to integrated poultry, swine, and cattle integrators, as well as through commercial animal feed manufacturers, wholesalers, and distributors. The company was formerly known as Philipp Brothers Chemicals, Inc. and changed its name to Phibro Animal Health Corporation in July 2003. Phibro Animal Health Corporation was founded in 1946 and is headquartered in Teaneck, New Jersey.
Portola Pharmaceuticals logo

Portola Pharmaceuticals

NASDAQ:PTLA
Portola Pharmaceuticals, Inc., a biopharmaceutical company, develops and commercializes novel therapeutics in the areas of thrombosis and other hematologic disorders and inflammation in the United States. The company offers Andexxa, an antidote for patients treated with rivaroxaban and apixaban when reversal of anticoagulation is needed due to life-threatening or uncontrolled bleeding; and Bevyxxa (betrixaban), an oral, once-daily Factor Xa inhibitor for the prevention of venous thromboembolism in adult patients hospitalized for an acute medical illness. It is also advancing cerdulatinib, a dual spleen tyrosine kinase and janus kinases inhibitor in development for the treatment of hematologic cancers. In addition, the company is developing PRT2761, a Syk inhibitor that has completed Phase II clinical trial for the treatment for allergic conjunctivitis. Portola Pharmaceuticals, Inc. has collaboration agreements with Bristol-Myers Squibb; Pfizer Inc.; Bayer Pharma, AG; Janssen Pharmaceuticals, Inc.; Daiichi Sankyo, Inc.; Millennium Pharmaceuticals, Inc.; SRX Cardio; LLC; Ora; and Astellas Pharma Inc. The company was founded in 2003 and is headquartered in South San Francisco, California.
Rocket Pharmaceuticals logo

Rocket Pharmaceuticals

NASDAQ:RCKT
Rocket Pharmaceuticals, Inc., together with its subsidiaries, operates as a late-stage biotechnology company that focuses on developing gene therapies for rare and devastating diseases. It has three clinical-stage ex vivo lentiviral vector programs for fanconi anemia, a genetic defect in the bone marrow that reduces production of blood cells or promotes the production of faulty blood cells; leukocyte adhesion deficiency-I, a genetic disorder that causes the immune system to malfunction; and pyruvate kinase deficiency, a rare red blood cell autosomal recessive disorder that results in chronic non-spherocytic hemolytic anemia. The company also has a clinical stage in vivo adeno-associated virus program for Danon disease, a multi-organ lysosomal-associated disorder leading to early death due to heart failure; Plakophilin-2 Arrhythmogenic Cardiomyopathy, an inheritable cardiac disorder; and BAG3 Dilated Cardiomyopathy. It has license agreements with Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, Centro de Investigacion Biomedica En Red, and Fundacion Instituto de investigacion Sanitaria Fundacion Jimenez Diaz; UCL Business PLC; The Regents of the University of California; and REGENXBIO, Inc. Rocket Pharmaceuticals, Inc. was founded in 1999 and is headquartered in Cranbury, New Jersey.